Latest news with #BEAM
Yahoo
30-05-2025
- Business
- Yahoo
FDA Grants Orphan Drug Status to Beam Therapeutics Inc. (BEAM)' AATD Gene Therapy
Beam Therapeutics Inc. (NASDAQ:BEAM) has secured U.S. FDA orphan drug designation for BEAM-302, its pioneering genetic medicine targeting alpha-1 antitrypsin deficiency (AATD), a rare inherited disorder that can cause severe lung and liver disease. BEAM-302, delivered via liver-targeting lipid nanoparticles, is designed to correct the underlying DNA mutation responsible for AATD, offering hope for a one-time, potentially curative treatment. This regulatory milestone follows the recent Regenerative Medicine Advanced Therapy (RMAT) designation, underscoring the therapy's promise and the urgent need for effective AATD solutions. A biotechnologist in a lab coat discussing a therapeutic antibody with a colleague. Preliminary data from ongoing Phase 1/2 trials show BEAM-302 is well tolerated and achieves dose-dependent, durable correction of the disease-causing mutation, with protein levels exceeding therapeutic thresholds in the 60 mg dose group. Dosing in higher cohorts is underway, with more results from Beam Therapeutics Inc. (NASDAQ:BEAM) expected later in 2025. Orphan drug designation brings significant benefits, including tax credits, user fee exemptions, and up to seven years of market exclusivity post-approval, accelerating development for this first-in-class base editing therapy for AATD, a condition with no current curative treatments. While we acknowledge the potential of BEAM to grow, our conviction lies in the belief that some AI stocks hold greater promise for delivering higher returns and have limited downside risk. If you are looking for an AI stock that is more promising than BEAM and that has 100x upside potential, check out our report about this READ NEXT: and Disclosure: None. Error in retrieving data Sign in to access your portfolio Error in retrieving data Error in retrieving data Error in retrieving data Error in retrieving data
Business Insider
29-05-2025
- Business
- Business Insider
Beam Therapeutics treatment of alpha-1 antitrypsin deficiency gets orphan status
Beam Therapeutics (BEAM)' treatment of alpha-1 antitrypsin deficiency was granted FDA orphan designation status, according to a post to the agency's website. Confident Investing Starts Here: Easily unpack a company's performance with TipRanks' new KPI Data for smart investment decisions Receive undervalued, market resilient stocks right to your inbox with TipRanks' Smart Value Newsletter Published first on TheFly – the ultimate source for real-time, market-moving breaking financial news. Try Now>>
Yahoo
14-05-2025
- General
- Yahoo
Hinds County to host meetings on bridging digital divide
HINDS COUNTY, Miss. (WJTV) – Hinds County residents are encouraged to attend community meetings about a 'growing communications emergency' that's affecting rural parts of the county. According to Hinds County leaders, the combination of accelerating copper wire theft, the phase-out of traditional landline services, and inadequate broadband infrastructure has left many residents without any reliable means of communication. Mississippi College, Christ Covenant partnership offers college-level math course 'These are not future concerns—we are already seeing people cut off from the outside world,' said Felicia Tripp, Hinds County Broadband Coordinator. 'We must act now to ensure no one in Hinds County is left behind.' (All meetings begin at 6:00 p.m.) Raymond – Monday, May 19, at Bellmont Missionary Baptist Church Utica – Tuesday, May 20, at the Utica Community Center Terry – Thursday, May 22, at the Town of Terry Community Center Edwards – Thursday, May 29, at Ratliff Missionary Baptist Church Officials said the meetings will serve as both public forums and action-planning sessions to address the digital divide and determine how programs like BEAD (Broadband Equity, Access, and Deployment) and BEAM (Broadband Expansion and Accessibility of Mississippi) can be leveraged more effectively to serve Hinds County communities. Close Thanks for signing up! Watch for us in your inbox. Subscribe Now Copyright 2025 Nexstar Media, Inc. All rights reserved. This material may not be published, broadcast, rewritten, or redistributed.
Channel Post MEA
10-04-2025
- Business
- Channel Post MEA
Bimser Establishes New Regional Office In Dubai
Turkish enterprise software company, Bimser, with over 2,500 global customers and more than a quarter of a century of experience, has officially opened its new regional office in Dubai. This marks a significant step in the company's strategic expansion plan aimed at deepening its presence across the Middle East and North Africa (MENA). Founded in 1998, Bimser is a key player in the enterprise software sector, offering a range of solutions including it's low-code platform Synergy, quality management system QDMS, asset and maintenance management platform BEAM, performance management tool Ensemble, and governance, risk and compliance tool QGRC. The company serves customers in over 30 countries, with offices in Türkiye, the United States, and now the United Arab Emirates. 'Our goal is to become a global company, and establishing a presence in Dubai is a strategic move in that journey,' said Murat Atıcı, CEO of Bimser. 'The MENA region represents significant opportunities, and this office allows us to support our customers and partners more effectively with a dedicated local team.' The Dubai office will serve as a marketing and sales hub for the region, managing both partner and customer relationships. Bimser plans to leverage its partner-focused go-to-market model, aiming to triple the number of active partners in the Gulf by the end of the year. The UAE market is the company's initial focus, where it already has three partners, including a strong Dubai-based firm with ties to Saudi Arabia. Wellspring Solutions, Expert House SP, Jacky's Business Solutions, IT-SBO, Eco-Tech, ZingerStick Software, and IISolutions are some Bimser's active partners in the region. 'Our solutions are not tied to a specific industry — we have deep experience across 20+ different sectors. What we're bringing to the region is flexibility, scalability, and localised support,' added Atıcı. The move aligns with the rapid growth of enterprise software in the Middle East. According to IDC, the global enterprise applications market is forecast to surpass $600 billion by 2028, with strong momentum in the MENA region driven by digital transformation, regulatory compliance, and the shift toward cloud-based platforms. 0 0
Tahawul Tech
10-04-2025
- Business
- Tahawul Tech
Bimser opens UAE office to expand regional operations
Turkish enterprise software company, Bimser, with over 2,500 global customers and more than a quarter of a century of experience, has officially opened its new regional office in Dubai. This marks a significant step in the company's strategic expansion plan aimed at deepening its presence across the Middle East and North Africa (MENA). Founded in 1998, Bimser is a key player in the enterprise software sector, offering a range of solutions including it's low-code platform Synergy, quality management system QDMS, asset and maintenance management platform BEAM, performance management tool Ensemble, and governance, risk and compliance tool QGRC. The company serves customers in over 30 countries, with offices in Türkiye, the United States, and now the United Arab Emirates. 'Our goal is to become a global company, and establishing a presence in Dubai is a strategic move in that journey', said Murat Atıcı, CEO of Bimser. 'The MENA region represents significant opportunities, and this office allows us to support our customers and partners more effectively with a dedicated local team'. The Dubai office will serve as a marketing and sales hub for the region, managing both partner and customer relationships. Bimser plans to leverage its partner-focused go-to-market model, aiming to triple the number of active partners in the Gulf by the end of the year. The UAE market is the company's initial focus, where it already has three partners, including a strong Dubai-based firm with ties to Saudi Arabia. Wellspring Solutions, Expert House SP, Jacky's Business Solutions, IT-SBO, Eco-Tech, ZingerStick Software, and IISolutions are some Bimser's active partners in the region. 'Our solutions are not tied to a specific industry — we have deep experience across 20+ different sectors. What we're bringing to the region is flexibility, scalability, and localised support', added Atıcı. The move aligns with the rapid growth of enterprise software in the Middle East. According to IDC, the global enterprise applications market is forecast to surpass $600 billion by 2028, with strong momentum in the MENA region driven by digital transformation, regulatory compliance, and the shift toward cloud-based platforms. Image Credit: Bimser
