Children's Hospital LA halts use of Sarepta's gene therapy for all patients
Elevidys was granted full FDA approval last year for children with Duchenne Muscular Dystrophy who can still walk, and received conditional approval for non-ambulatory patients. However, Sarepta suspended use in non-ambulatory cases in June, after two teenagers died of liver failure following treatment.The FDA's recent request reignited scrutiny of the therapy's safety profile. Shares of Sarepta, down about 90% year-to-date, fell 5% on Monday to close at $13.32 on Nasdaq.- EndsWith inputs from Reuters
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