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Sarepta Announces Voluntary Pause of Elevidys Shipments in US

Sarepta Announces Voluntary Pause of Elevidys Shipments in US

Bloomberg3 days ago
Sarepta Therapeutics Inc. announced that the company plans to temporarily pause all shipments of its gene therapy to treat Duchenne muscular dystrophy, Elevidys, in a reversal of its prior stance.
The Food and Drug Administration asked Sarepta to pause shipments of the drug on Friday following news reports of a patient death in a clinical trial for another Sarepta therapy that works in a similar way. The company initially refused, which drew backlash.
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