Latest news with #LCATDeficiency
Business Wire
28-05-2025
- Business
- Business Wire
ABIONYX Pharma Provides an Update on Its Activity and Cash Position for the 1 st Quarter 2025
TOULOUSE, France & LAKELAND, Mich.--(BUSINESS WIRE)--Regulatory News: ABIONYX Pharma (FR0012616852 - ABNX - PEA PME eligible), a new generation biotech company dedicated to the discovery and development of innovative therapies based on the world's only natural recombinant apoA-I, today provides an update on its activity and cash position as of March 31, 2025. Selected financial information (IFRS) ABIONYX Pharma recorded consolidated quarterly sales of nearly €1 million in Q1 2025, down on Q1 2024. This decline is cyclical and reflects a wait-and-see attitude on the part of customers in the context of uncertain US customs policy. In the business dedicated to the discovery and development of innovative therapies designed to improve patients' lives, the Company generated no sales in the quarter, as ABIONYX Pharma continues to provide its bioproduct free of charge in the context of compassionate access applications. As at March 31, 2025, the Company had cash and cash equivalents of nearly €4.1 million, before receipt of the estimated €1.08 million Research Tax Credit and after receipt of the first €2.17 million tranche of France 2030 funding. R&D update and anticipated key milestones: Concerning the rare disease known as 'LCAT Deficiency' (Lecithin Cholesterol Acyl-Transferase deficiency or Norum disease), the Company continues to receive new requests for Compassionate Access Authorization (CAA) for recombinant apoA-I, CER-001, from several hospitals around the world. Last May, ABIONYX Pharma sent the European Medicines Agency (EMA) the clinical results of treated patients, with a view to continuing discussions and obtaining feedback for a future application for Compassionate Access. With regard to sepsis, ABIONYX Pharma is pursuing its strategic plan to find a strategic partner for its biomedicine. About ABIONYX Pharma ABIONYX Pharma is a next-generation biotech company focused on developing innovative medicines for diseases where there is no effective or existing treatment, even the rarest ones. The company expedites the development of novel therapeutics through an extensive expertise in lipid science and a differentiated apoA-I-based technology platform. ABIONYX Pharma is committed to radically improving treatment outcomes in Sepsis and critical care.
Associated Press
28-02-2025
- Business
- Associated Press
World Rare Disease Day: ABIONYX renews its commitment to treat LCAT Deficiency (Norum's disease) and provides an update on its advances
TOULOUSE, France & LAKELAND, Mich.--(BUSINESS WIRE)--Feb 28, 2025-- ABIONYX Pharma, (FR0012616852 - ABNX - eligible for PEA PME), a next generation biopharma company dedicated to the development of innovative biomedicines based on a recombinant apolipoprotein apoA-1 for the treatment of the most severe inflammatory diseases, today provides an update on its progress and confirms its commitment to the rare disease known as LCAT Deficiency or 'Norum's disease'. About ABIONYX Pharma ABIONYX Pharma is a next-generation biopharma company dedicated to the development of innovative biomedicines for the most severe inflammatory diseases for which there is no effective or existing treatment, even in the rarest indications. The company accelerates the development of breakthrough therapies thanks to in-depth expertise in lipid science and a technological platform based on recombinant apoA-I. ABIONYX Pharma is committed to radically improving the results of sepsis treatments and intensive care. CONTACT: NewCap Investor relations Nicolas Fossiez Louis-Victor Delouvrier [email protected] +33 (0)1 44 71 98 53NewCap Media relations Arthur Rouillé +33 (0)1 44 71 00 15 KEYWORD: MICHIGAN EUROPE UNITED STATES NORTH AMERICA FRANCE SOURCE: ABIONYX Pharma Copyright Business Wire 2025. PUB: 02/28/2025 01:30 AM/DISC: 02/28/2025 01:30 AM
