Doctors rewrite baby's DNA to cure genetic disorder in world first
A baby with an extremely rare and life-threatening genetic disorder has had its DNA rewritten by doctors in a world first that could pave the way for more personalised gene-editing therapies.
Independent experts have hailed the breakthrough as 'totally extraordinary' after doctors were able to treat a severe disorder that is suffered by only one in 1.3 million people and kills half of those affected in infancy.
The baby, known as KJ, was born with a condition known as carbamoyl phosphate synthetase 1, or CPS1, deficiency.
• Hopes rise of a cheap cure for rare genetic diseases
Ammonia is created in the body when proteins are processed in the liver. An enzyme in the liver is meant to break this ammonia down into urea, which
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